Dr. Xiao Xiao

PhD,Co-founder & Chief Science Officer, Belief BioMed; Pioneer in Gene Therapy

Leadership & Innovation

  • Co-founder & CSO. Belief BioMed (China): Leading development of China’s first potential gene therapy drug for hemophilia B, currently in Phase III
    trials and nearing BLA submission.
  • Co-founder, AskBio and Bamboo Therapeutics (U.S.): Spearheaded advancements in AAV-based gene therapies.
  • Co-founder. Rui-ou (瑞) Charitable Foundation: Advancing rare disease research and translational medicine.
    Academic & Professional Credentials
  • Ph.D., University of Pittsburgh (1992).
  • Distinguished Professor, Eshelman School of Pharmacy, University of North Carolina at Chapel Hill.
  • Adjunct Professor, East China University of Science and Technology (Bioengineering/Pharmacy).
  • Board Member, American Society of Gene and Cell Therapy (ASGCT).
  • Lifetime Member. Chinese Society of Biologists.
  • NIH Grant Reviewer, Editorial Roles: Key journals in gene therapy

Research Impact

  • Focus : Gene delivery vectors and therapies for Duchenne muscular dystrophy, hemophilia, lysosomal storage disorders, and age-related diseases.
  • Publications: 230+ papers (*Nature, Science Translational Medicine*), 20,000+ citations. – Clinical Translation: Hemophilia B gene therapy drug (Phase
    III) poised to become China’s first approved gene therapy for genetic disorders

Entrepreneurial Vision

  • Bridged academic research with commercialization, co-founding multiple biotech firms to accelerate gene therapy from lab to clinic.
  • Advocated for global collaboration in rare disease research through philanthropy and cross-border partnerships

Legacy :

A trailblazer in gene therapy, driving scientific innovation and equitable access to transformative treatments worldwide.